Rare Disease

Showing 17–27 of 27 results

• 

  POMBILITI (cipaglucosidase alfa-atga)

  Read more
• 

  RIVFLOZA (nedosiran)

  Read more
• 

  RYSTIGGO (rozanolixizumab-noli)

  Read more
• 

  RYTELO (imetelstat) for injection

  Read more
• 

  RYZNEUTA (efbemalenograstim alfa-vuxw)

  Read more
• 

  TEVIMBRA (tislelizumab-jsgr) injection

  Read more
• 

  VEOPOZ (pozelimab-bbfg)

  Read more
• 

  VONVENDI (recombinant) lyophilized powder for solution

  Read more
• 

  VORANIGO (vorasidenib) tablets

  Read more
• 

  Wainua

  Read more
• 

  WINREVAIR (sotatercept-csrk) for injection

  Read more